Infant With Incurable Disease is First to Successfully Receive Personalized Gene Therapy Treatment

In a historic medical breakthrough, a child diagnosed with a rare genetic disorder has been successfully treated with a customized CRISPR gene editing therapy by a team at Children’s Hospital of Philadelphia and Penn Medicine. The infant, KJ, was born with a rare metabolic disease known as severe carbamoyl phosphate synthetase deficiency (CPS1). After spending […] The post Infant With Incurable Disease is First to Successfully Receive Personalized Gene Therapy Treatment appeared first on Good News Network.

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